What are the causes of leukopenia?

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Causes of Leukopenia

Leukopenia is primarily caused by decreased neutrophil production, increased destruction, or excessive sequestration, with the most common etiologies being infections, medications, malignancies, and autoimmune disorders. 1

Definition and Classification

Leukopenia is defined as a reduction in circulating white blood cells, particularly when the absolute neutrophil count (ANC) falls below 1,500 cells/mm³. It can be classified as:

  • Mild: 1,000-1,500 cells/mm³
  • Moderate: 500-1,000 cells/mm³
  • Severe: <500 cells/mm³ 2

The severity and duration of leukopenia directly correlate with infection risk, with severe neutropenia (<500 cells/mm³) significantly increasing susceptibility to bacterial and fungal infections 3.

Major Causes of Leukopenia

1. Infections

  • Viral infections: Most common cause of transient leukopenia, especially in children 4
    • HIV, hepatitis, CMV, EBV
    • Respiratory syncytial virus (RSV), parainfluenza, influenza A and B 5
  • Bacterial infections:
    • Typhoid fever, tuberculosis
    • Gram-negative infections (E. coli, Klebsiella, Enterobacter, Pseudomonas) 5
    • Overwhelming bacterial sepsis

2. Medications

  • Chemotherapeutic agents: Major cause of predictable, dose-dependent leukopenia
  • Immunosuppressants: Azathioprine, mycophenolate
  • Antipsychotics: Clozapine
  • Antibiotics: Trimethoprim-sulfamethoxazole, beta-lactams
  • Anticonvulsants: Carbamazepine, valproic acid

3. Hematologic Malignancies

  • Leukemias: Acute myeloid leukemia, hairy cell leukemia 5
  • Myelodysplastic syndromes
  • Lymphomas: With bone marrow infiltration
  • Multiple myeloma

4. Autoimmune Disorders

  • Systemic lupus erythematosus
  • Rheumatoid arthritis
  • Autoimmune neutropenia
  • Felty's syndrome

5. Bone Marrow Failure Syndromes

  • Aplastic anemia
  • Congenital neutropenias
  • Large granular lymphocytic leukemia

6. Splenic Sequestration

  • Hypersplenism from portal hypertension, lymphoma, or myelofibrosis
  • Cirrhosis with portal hypertension 5

7. Nutritional Deficiencies

  • Vitamin B12 deficiency
  • Folate deficiency
  • Copper deficiency
  • Severe malnutrition

8. Cancer-Related Causes

  • Direct bone marrow infiltration by solid tumors
  • Radiation therapy affecting bone marrow
  • Post-chemotherapy myelosuppression 5
  • Paraneoplastic immune-mediated destruction

9. Congenital Disorders

  • Kostmann syndrome
  • Cyclic neutropenia
  • Shwachman-Diamond syndrome
  • Fanconi anemia

Special Considerations in Cancer Patients

Cancer patients are particularly susceptible to leukopenia due to:

  1. Myelosuppressive treatments: Chemotherapy and radiation therapy directly damage bone marrow stem cells 5

  2. Disruption of mucosal barriers: Chemotherapy and radiation impair mucosal immunity, allowing invasion by local flora 5

  3. Disease-related factors: Tumors may directly infiltrate bone marrow or cause paraneoplastic phenomena

  4. Malnutrition: Common in advanced malignancy, further increasing infection risk 5

Clinical Significance and Risk Assessment

The clinical significance of leukopenia depends on:

  • Severity: Risk increases dramatically with ANC <500 cells/mm³
  • Duration: Prolonged neutropenia carries higher risk
  • Rate of decline: Rapid falls indicate more severe underlying pathology
  • Bone marrow reserve: Reflected in the rate of decline and recovery 5

Common Pitfalls in Evaluation

  1. Failing to recognize neutropenic fever as a medical emergency requiring immediate broad-spectrum antibiotics 6

  2. Attributing leukopenia solely to medications without excluding other serious causes including underlying hematological malignancies 6

  3. Overlooking chronic lymphocytic leukemia (CLL) as a cause of recurrent infections due to hypogammaglobulinemia despite normal or elevated white cell counts 6

  4. Ignoring other cytopenias, as many conditions affect multiple cell lines 6

  5. Misinterpreting relative versus absolute leukopenia in patients with lymphocytosis

By understanding these diverse causes of leukopenia, clinicians can develop a systematic approach to diagnosis and management, focusing on the most likely etiologies based on clinical presentation, patient history, and associated findings.

References

Research

The etiology and management of leukopenia.

Canadian family physician Medecin de famille canadien, 1984

Research

Neutropenia: etiology and pathogenesis.

Clinical cornerstone, 2006

Research

How to approach neutropenia.

Hematology. American Society of Hematology. Education Program, 2012

Research

[Leucopenia in children].

Duodecim; laaketieteellinen aikakauskirja, 2011

Guideline

Guideline Directed Topic Overview

Dr.Oracle Medical Advisory Board & Editors, 2025

Guideline

Management of Leukopenia in Long COVID

Praxis Medical Insights: Practical Summaries of Clinical Guidelines, 2025

Professional Medical Disclaimer

This information is intended for healthcare professionals. Any medical decision-making should rely on clinical judgment and independently verified information. The content provided herein does not replace professional discretion and should be considered supplementary to established clinical guidelines. Healthcare providers should verify all information against primary literature and current practice standards before application in patient care. Dr.Oracle assumes no liability for clinical decisions based on this content.

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