What gene has the highest risk for early-onset Alzheimer's disease (AD)?

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Last updated: February 11, 2025View editorial policy

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From the Guidelines

The PSEN1 gene has the highest risk for early-onset Alzheimer's disease (AD) due to its complete penetrance, meaning that all individuals who have a PSEN1 mutation will develop AD if they live a normal lifespan 1.

Key Points

  • PSEN1, PSEN2, and APP are the three known deterministic genes associated with autosomal dominant early-onset AD (EOAD) 1.
  • Mutations in PSEN1 and APP are associated with complete penetrance, while mutations in PSEN2 show 95% penetrance 1.
  • The age of onset can vary more than 20 years within the same family, and clear genotype-phenotype correlations cannot typically be made for the three causative genes 1.
  • Genetic counseling and testing for AD should be offered in situations where a symptomatic individual has EOAD, or there is an autosomal dominant family history of dementia with one or more cases of EOAD 1.
  • The Alzheimer Disease & Frontotemporal Dementia Mutation Database should be consulted before disclosure of genetic test results, and specific genotypes should not be used to predict the phenotype in diagnostic or predictive testing 1.

From the Research

Gene Associated with Early-Onset Alzheimer's Disease

The gene with the highest risk for early-onset Alzheimer's disease (AD) is associated with mutations in the presenilin 1 (PSEN1) gene, as it is the most frequently mutated gene in autosomal dominant early-onset AD, with a mutation frequency of 18 to 50% 2.

Key Genes Involved in Early-Onset AD

Some of the key genes involved in early-onset AD include:

  • Amyloid precursor protein (APP)
  • Presenilin 1 (PSEN1)
  • Presenilin 2 (PSEN2) 3, 4, 5, 2, 6

Genetic Mutations and Risk

Mutations in these genes, particularly PSEN1, have been identified as major genetic causes of early-onset Alzheimer's disease (EOAD) 4. The apolipoprotein E (APOE) epsilon4 allele has also been identified as a risk factor for both late-onset and early-onset AD 3, 2.

Genetic Screening and Diagnosis

Genetic screening, including whole exome sequencing, has been successfully used to identify mutations and diagnose early-onset AD 4, 5. Understanding the genetic mechanisms of AD is essential for the development of diagnostic processes and therapeutic targets 3, 5, 6.

References

Guideline

Guideline Directed Topic Overview

Dr.Oracle Medical Advisory Board & Editors, 2025

Research

Genetics of early-onset Alzheimer dementia.

TheScientificWorldJournal, 2003

Research

The genetics of Alzheimer's disease.

Clinical interventions in aging, 2014

Research

The genetic landscape of Alzheimer disease.

Handbook of clinical neurology, 2018

Research

Alzheimer's Disease: An Updated Overview of Its Genetics.

International journal of molecular sciences, 2023

Professional Medical Disclaimer

This information is intended for healthcare professionals. Any medical decision-making should rely on clinical judgment and independently verified information. The content provided herein does not replace professional discretion and should be considered supplementary to established clinical guidelines. Healthcare providers should verify all information against primary literature and current practice standards before application in patient care. Dr.Oracle assumes no liability for clinical decisions based on this content.

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