What is the dosing for Vutrisiran (patisiran), a medication for hereditary transthyretin amyloidosis?

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Last updated: March 30, 2025View editorial policy

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From the Guidelines

Vutrisiran should be administered as a subcutaneous injection of 25 mg every 3 months, with no dose adjustments required for patients with mild to moderate renal or hepatic impairment, as recommended in the 2023 ACC expert consensus decision pathway on comprehensive multidisciplinary care for the patient with cardiac amyloidosis 1. The dosing regimen for Vutrisiran is straightforward, with a fixed dose of 25 mg administered subcutaneously every 3 months. This is in contrast to other treatments for hereditary transthyretin-mediated amyloidosis (hATTR), which may require more frequent administration. Key considerations for Vutrisiran administration include:

  • Injection site rotation to minimize local reactions
  • No requirement for dose adjustments in patients with mild to moderate renal or hepatic impairment
  • Monitoring for infusion-related reactions, although these are uncommon
  • Laboratory monitoring of vitamin A levels, with supplementation typically recommended due to the potential for decreased vitamin A levels resulting from TTR reduction. The mechanism of action of Vutrisiran, which involves silencing the production of transthyretin (TTR) protein through RNA interference, helps to reduce the accumulation of amyloid deposits in tissues, thereby slowing disease progression and potentially improving neurological and cardiac manifestations of hATTR amyloidosis, as noted in the context of comprehensive care for cardiac amyloidosis 1.

From the FDA Drug Label

The mean fraction of unchanged vutrisiran eliminated in urine was approximately 19. 4% at the recommended dose of 25 mg. Patients were randomized 3:1 to receive 25 mg of AMVUTTRA subcutaneously once every 3 months (N=122)

The recommended dosing of vutrisiran is 25 mg administered subcutaneously once every 3 months 2.

From the Research

Vutrisiran Dosing

  • Vutrisiran is administered subcutaneously at a dose of 25 mg every 3 months 3, 4
  • This dosing regimen has been shown to be effective in reducing neuropathy impairment and improving quality of life in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy 3, 4
  • The same dosing regimen has also been used in studies evaluating the efficacy and safety of vutrisiran in patients with transthyretin amyloidosis with cardiomyopathy, with results showing a lower risk of death from any cause and cardiovascular events compared to placebo 5
  • Additionally, vutrisiran has been shown to have a beneficial effect on exploratory cardiac parameters, including NT-proBNP and echocardiographic parameters, in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy 6

Key Findings

  • Vutrisiran 25 mg every 3 months has been consistently used as the dosing regimen in clinical trials 3, 4, 5, 6
  • This dosing regimen has been shown to be effective and well-tolerated in patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy and transthyretin amyloidosis with cardiomyopathy 3, 4, 5, 6
  • The efficacy and safety of vutrisiran have been evaluated in several clinical trials, with results supporting its use as a treatment option for these conditions 3, 4, 5, 6

References

Guideline

Guideline Directed Topic Overview

Dr.Oracle Medical Advisory Board & Editors, 2025

Research

Efficacy and safety of vutrisiran for patients with hereditary transthyretin-mediated amyloidosis with polyneuropathy: a randomized clinical trial.

Amyloid : the international journal of experimental and clinical investigation : the official journal of the International Society of Amyloidosis, 2023

Professional Medical Disclaimer

This information is intended for healthcare professionals. Any medical decision-making should rely on clinical judgment and independently verified information. The content provided herein does not replace professional discretion and should be considered supplementary to established clinical guidelines. Healthcare providers should verify all information against primary literature and current practice standards before application in patient care. Dr.Oracle assumes no liability for clinical decisions based on this content.

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