Can phenobarbitone (phenobarbital) cause myositis in patients, particularly those with a history of muscle disorders or on long-term therapy?

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Does Phenobarbitone Cause Myositis?

No, phenobarbitone (phenobarbital) does not cause myositis. The FDA-approved drug label for phenobarbital lists myalgic pain as a rare adverse effect, but myositis is not documented as a known complication 1.

Evidence from FDA Drug Labeling

The official phenobarbital prescribing information describes musculoskeletal adverse effects as follows:

  • Myalgic pain (muscle pain) may rarely occur, particularly in psychoneurotic patients with insomnia 1
  • This pain appears in paroxysms, is most intense in early morning hours, and typically affects the neck, shoulder girdle, and upper limbs 1
  • Symptoms may persist for days after drug discontinuation 1
  • Critically, myositis (muscle inflammation) is not listed among the adverse reactions 1

Distinction Between Myalgia and Myositis

This distinction is clinically important:

  • Myalgia = muscle pain without inflammation or weakness, with normal creatine kinase (CK) levels 2, 3
  • Myositis = inflammatory muscle disease characterized by proximal muscle weakness, markedly elevated CK levels (often >10x normal), abnormal EMG findings, and muscle edema on MRI 2, 3

Phenobarbital causes the former (pain), not the latter (inflammatory disease) 1.

Other Documented Phenobarbital Toxicities

Long-term phenobarbital use is associated with:

  • CNS effects: sedation, behavioral problems, hyperactivity, and rarely dementia 1, 4
  • Hypersensitivity syndrome: fever, rash, lymphadenopathy, and hematologic abnormalities including thrombocytopenia 5
  • Megaloblastic anemia with chronic use 1
  • Respiratory depression and circulatory collapse in overdose 1, 6

Muscle twitching can paradoxically occur with phenobarbital toxicity (not myositis), representing a manifestation of drug toxicity rather than seizure recurrence 7.

Clinical Pitfall to Avoid

If a patient on phenobarbital develops true proximal muscle weakness with elevated CK, do not attribute this to phenobarbital. Instead, investigate alternative causes:

  • Statin-induced necrotizing myopathy (if on concurrent statins) 2
  • Autoimmune inflammatory myositis (polymyositis, dermatomyositis) 2, 3, 8
  • Proton pump inhibitor-associated myopathy (if on concurrent PPIs) 9
  • Paraneoplastic myositis 2

The diagnostic workup should include CK measurement, myositis-specific autoantibodies, EMG, and MRI imaging to establish the correct diagnosis 2, 3, 8.

References

Guideline

Guideline Directed Topic Overview

Dr.Oracle Medical Advisory Board & Editors, 2025

Guideline

Differentiating Viral Myositis from Autoimmune Myositis in Teenagers

Praxis Medical Insights: Practical Summaries of Clinical Guidelines, 2026

Research

Side effects of phenobarbital and phenytoin during long-term treatment of epilepsy.

Acta neurologica Scandinavica. Supplementum, 1983

Research

Antiepileptic Hypersensitivity Syndrome to Phenobarbital: A Case Report.

Iranian journal of allergy, asthma, and immunology, 2019

Research

Acute phenobarbital intoxication.

Southern medical journal, 1992

Guideline

Inflammatory Myositis Diagnosis and Management

Praxis Medical Insights: Practical Summaries of Clinical Guidelines, 2025

Professional Medical Disclaimer

This information is intended for healthcare professionals. Any medical decision-making should rely on clinical judgment and independently verified information. The content provided herein does not replace professional discretion and should be considered supplementary to established clinical guidelines. Healthcare providers should verify all information against primary literature and current practice standards before application in patient care. Dr.Oracle assumes no liability for clinical decisions based on this content.

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