Does hydroxyurea cause decreased appetite?

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Hydroxyurea and Decreased Appetite

Yes, hydroxyurea does cause decreased appetite (anorexia), which is listed as a recognized gastrointestinal adverse effect of this medication. 1, 2

Evidence from Guidelines

The most authoritative evidence comes from the American Academy of Dermatology-National Psoriasis Foundation guidelines, which explicitly list anorexia (decreased appetite) among the gastrointestinal toxicities of hydroxyurea, alongside stomatitis, nausea, vomiting, diarrhea, and constipation. 1 This guideline represents expert consensus based on established clinical experience with the drug.

Supporting Clinical Evidence

  • Case reports document anorexia as a presenting symptom in patients experiencing hydroxyurea toxicity. In one published case, an 82-year-old male developed anorexia along with nausea, vomiting, and fever within 8 days of starting hydroxyurea 500 mg three times weekly for polycythemia vera. 3

  • When the drug was discontinued, symptoms resolved within 2 days, and when restarted, the patient again developed nausea and anorexia 10 days later, establishing a clear temporal relationship. 3

  • Multiple reviews confirm anorexia as a recognized side effect of hydroxyurea therapy across different indications, including sickle cell disease and myeloproliferative disorders. 2, 4

Clinical Context and Mechanism

The gastrointestinal effects, including decreased appetite, likely result from hydroxyurea's mechanism as a ribonucleotide reductase inhibitor that affects rapidly dividing cells, including those in the gastrointestinal mucosa. 4, 5 These effects are generally dose-dependent and reversible with drug discontinuation or dose reduction. 3

Important Clinical Considerations

  • Anorexia may be an early warning sign of hydroxyurea toxicity, particularly when accompanied by other gastrointestinal symptoms (nausea, vomiting) or constitutional symptoms (fever, fatigue). 3

  • The symptom is typically reversible upon discontinuation of the medication, with resolution occurring within days. 3

  • Patients should be counseled about this potential side effect when initiating therapy, as it may affect medication adherence and nutritional status during treatment. 3

References

Guideline

Guideline Directed Topic Overview

Dr.Oracle Medical Advisory Board & Editors, 2025

Research

Hydroxyurea in sickle cell disease: drug review.

Indian journal of hematology & blood transfusion : an official journal of Indian Society of Hematology and Blood Transfusion, 2014

Research

Hydroxyurea induced acute elevations in liver function tests.

Journal of oncology pharmacy practice : official publication of the International Society of Oncology Pharmacy Practitioners, 2008

Research

Hydroxyurea: a key player in cancer chemotherapy.

Expert review of anticancer therapy, 2012

Professional Medical Disclaimer

This information is intended for healthcare professionals. Any medical decision-making should rely on clinical judgment and independently verified information. The content provided herein does not replace professional discretion and should be considered supplementary to established clinical guidelines. Healthcare providers should verify all information against primary literature and current practice standards before application in patient care. Dr.Oracle assumes no liability for clinical decisions based on this content.

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