Do male offspring develop disease in mitochondrial (mtDNA) inheritance?

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Last updated: February 28, 2025View editorial policy

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From the Guidelines

Male offspring can develop diseases in mitochondrial inheritance, but they cannot transmit the mitochondrial mutation to their children. Mitochondrial diseases are passed from mother to all her children, regardless of sex, because mitochondrial DNA is inherited exclusively from the mother [ 1 ]. When a mother carries a mitochondrial mutation, both her sons and daughters have an equal chance of inheriting the defective mitochondria. The severity of mitochondrial diseases can vary widely among siblings due to heteroplasmy (different proportions of normal and mutated mitochondria in different cells) [ 1 ].

Some key points to consider in mitochondrial inheritance include:

  • Mitochondrial DNA is inherited exclusively from the mother [ 1 ]
  • Male offspring can develop the disease, but they cannot transmit the mitochondrial mutation to their children
  • The severity of mitochondrial diseases can vary widely among siblings due to heteroplasmy [ 1 ]
  • Common mitochondrial disorders that affect males include Leber's hereditary optic neuropathy (LHON), mitochondrial encephalomyopathy with lactic acidosis and stroke-like episodes (MELAS), and Leigh syndrome [ 1 ]

In terms of management and counseling, it is essential to consider the unique aspects of mitochondrial inheritance, including the risk of transmission to offspring and the potential for variable expression of the disease [ 1 ]. Genetic counseling plays a crucial role in helping families understand the risks and implications of mitochondrial disease [ 1 ].

From the Research

Mitochondrial DNA Inheritance and Disease Development in Male Offspring

  • Mitochondrial diseases are relatively frequent and can be caused by maternally inherited mitochondrial DNA (mtDNA) mutations, with about 15% of cases attributed to this cause 2.
  • The severity of the phenotype and the lack of effective treatment make it crucial for couples to prevent the transmission of these mtDNA disorders to their offspring 2.
  • Preimplantation genetic diagnosis (PGD) is a viable option for preventing the transmission of mtDNA disorders, allowing for the transfer of embryos with a mutation load below the threshold of clinical expression 2.
  • Studies have shown that PGD can provide carriers of mtDNA mutations the opportunity to conceive healthy offspring, including male offspring 2.
  • However, the pattern of mitochondrial inheritance is not entirely clear, and there is evidence to suggest that paternal mitochondrial DNA transmission may occur in some cases, although this is not a common phenomenon 3, 4.
  • In cases where paternal mtDNA transmission does occur, it may follow an autosomal dominant-like inheritance mode, with biparental mtDNA transmission observed in some families 4.
  • The development of disease in male offspring due to mtDNA inheritance is still not fully understood and requires further research to elucidate the underlying mechanisms and to develop effective therapeutic strategies 5.
  • It is essential to note that mitochondrial transmission can be distinguished from X-linked transmission by examining sex-specific patterns of disease expression in matrilineally transmitted diseases 6.

References

Guideline

Guideline Directed Topic Overview

Dr.Oracle Medical Advisory Board & Editors, 2025

Research

Biparental inheritance of mitochondrial DNA in humans is not a common phenomenon.

Genetics in medicine : official journal of the American College of Medical Genetics, 2019

Research

Biparental Inheritance of Mitochondrial DNA in Humans.

Proceedings of the National Academy of Sciences of the United States of America, 2018

Research

Maternal transmission of mitochondrial diseases.

Genetics and molecular biology, 2020

Professional Medical Disclaimer

This information is intended for healthcare professionals. Any medical decision-making should rely on clinical judgment and independently verified information. The content provided herein does not replace professional discretion and should be considered supplementary to established clinical guidelines. Healthcare providers should verify all information against primary literature and current practice standards before application in patient care. Dr.Oracle assumes no liability for clinical decisions based on this content.

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