What medications can cause macrocytosis?

Medical Advisory BoardAll articles are reviewed for accuracy by our Medical Advisory Board
Educational purpose only • Exercise caution as content is pending human review
Article Review Status
Submitted
Under Review
Approved

Last updated: July 25, 2025View editorial policy

Personalize

Help us tailor your experience

Which best describes you? Your choice helps us use language that's most understandable for you.

Common Medications That Cause Macrocytosis

The most common medications that cause macrocytosis include methotrexate, azathioprine, 6-mercaptopurine, phenytoin, valproate, zidovudine, and other immunosuppressive agents. These medications can lead to macrocytosis through various mechanisms, often without causing anemia.

Mechanism-Based Classification of Medications Causing Macrocytosis

1. Medications Affecting Folate Metabolism

  • Methotrexate: Inhibits dihydrofolate reductase, preventing conversion of dihydrofolic acid to tetrahydrofolic acid 1
  • Sulfasalazine: Causes folate malabsorption 1
  • Trimethoprim/Sulfamethoxazole (TMP/SMX): Interferes with folate metabolism

2. Immunosuppressive Medications

  • Azathioprine: Causes macrocytosis through myelosuppressive activity 1
  • 6-Mercaptopurine: Similar to azathioprine, induces macrocytosis through bone marrow effects 1
  • Mycophenolate mofetil: Immunosuppressant that can affect cell maturation

3. Anticonvulsants

  • Phenytoin: Can cause macrocytosis and megaloblastic anemia, often responding to folate therapy 2
  • Valproate: Commonly causes macrocytosis in pediatric and adult populations 3

4. Antiretroviral Medications

  • Zidovudine (AZT): Frequently causes macrocytosis, especially in HIV patients 3

5. Other Medications

  • Hydroxyurea: Used in psoriasis and other conditions, affects DNA synthesis 1
  • Leflunomide: Can contribute to macrocytosis when used with other DMARDs 4

Clinical Significance and Monitoring

Medication-induced macrocytosis may present with or without anemia. In a study of patients with macrocytosis, 35% of cases were attributed to medication use 3. Importantly, only 20% of patients with medication-induced macrocytosis had concurrent anemia 4.

Monitoring Recommendations:

  • For patients on methotrexate: Regular CBC monitoring; consider folate supplementation (5 mg once weekly 24-72 hours after methotrexate, or 1 mg daily for 5 days per week) 1
  • For patients on sulfasalazine: Monitor for folate deficiency; supplementation with either folic or folinic acid may be needed 1
  • For patients on azathioprine or 6-mercaptopurine: Monitor CBC regularly as these can cause pancytopenia in addition to macrocytosis 5

Important Clinical Considerations

  1. Differential Diagnosis: When macrocytosis is detected, it's important to rule out other causes including:

    • Vitamin B12 deficiency
    • Folate deficiency
    • Alcoholism
    • Liver disease
    • Hypothyroidism
    • Myelodysplastic syndromes 6
  2. Persistent Unexplained Macrocytosis: Requires follow-up as approximately 11.6% of patients with unexplained macrocytosis may develop primary bone marrow disorders 7

  3. Medication Combinations: The risk of macrocytosis increases with combination therapy, particularly when using multiple DMARDs together 4

  4. Monitoring Frequency: For patients on high-risk medications, CBC monitoring should be performed:

    • Initially: Every 2-4 weeks
    • Maintenance: Every 1-3 months depending on medication stability

Recognizing medication-induced macrocytosis is important as it may be an early indicator of drug toxicity or, in some cases like methotrexate therapy, may actually correlate with treatment efficacy 4.

Professional Medical Disclaimer

This information is intended for healthcare professionals. Any medical decision-making should rely on clinical judgment and independently verified information. The content provided herein does not replace professional discretion and should be considered supplementary to established clinical guidelines. Healthcare providers should verify all information against primary literature and current practice standards before application in patient care. Dr.Oracle assumes no liability for clinical decisions based on this content.

Have a follow-up question?

Our Medical A.I. is used by practicing medical doctors at top research institutions around the world. Ask any follow up question and get world-class guideline-backed answers instantly.