What medications can cause macrocytosis?

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Medications That Cause Macrocytosis

Multiple medications can cause macrocytosis, most commonly methotrexate, azathioprine, 6-mercaptopurine, phenytoin, valproate, zidovudine, hydroxyurea, and sulfasalazine. 1

Common Medication Causes of Macrocytosis

Folate Antagonists and Metabolism Disruptors

  • Methotrexate: Inhibits dihydrofolate reductase, preventing conversion of dihydrofolic acid to tetrahydrofolic acid 1
  • Sulfasalazine: Causes folate malabsorption 1

Immunosuppressants

  • Azathioprine: Causes macrocytosis through myelosuppressive activity 2, 1
  • 6-Mercaptopurine: Induces macrocytosis through bone marrow effects 1

Anticonvulsants

  • Phenytoin: Associated with macrocytosis and megaloblastic anemia, which usually responds to folic acid therapy 3
  • Valproate: Affects DNA synthesis leading to macrocytosis 1

Other Medications

  • Hydroxyurea: Affects DNA synthesis in patients with psoriasis and other conditions 1
  • Zidovudine: Commonly causes macrocytosis in HIV patients 1, 4

Mechanisms of Medication-Induced Macrocytosis

  1. Folate antagonism: Medications like methotrexate directly interfere with folate metabolism
  2. Bone marrow suppression: Azathioprine and 6-mercaptopurine affect bone marrow function 2, 1
  3. DNA synthesis disruption: Hydroxyurea and zidovudine interfere with DNA synthesis
  4. Folate malabsorption: Sulfasalazine reduces folate absorption 1

Clinical Considerations

Monitoring Recommendations

  • For patients on methotrexate: Regular CBC monitoring and consider folate supplementation (5 mg once weekly 24-72 hours after methotrexate, or 1 mg daily for 5 days per week) 1
  • For patients on sulfasalazine: Monitor for folate deficiency and consider supplementation 1
  • For patients on hydroxyurea: Regular CBC monitoring 1

Important Distinctions

  • Macrocytosis from medications may occur with or without anemia
  • In thiopurine (azathioprine, 6-mercaptopurine) users, macrocytosis may be an early sign of bone marrow toxicity 2
  • Phenytoin can cause both macrocytosis and megaloblastic anemia that typically responds to folic acid therapy 3

Pitfalls and Caveats

  • Macrocytosis may be the first sign of medication toxicity before development of cytopenias 5
  • Medication-induced macrocytosis must be distinguished from other causes such as vitamin B12/folate deficiency, alcoholism, liver disease, and primary bone marrow disorders 6
  • Some patients on long-term azathioprine may develop severe megaloblastic anemia with pancytopenia even after years of stable therapy 7, 8
  • In pediatric populations, anticonvulsants, zidovudine, and immunosuppressants account for approximately 24% of macrocytosis cases 4

When evaluating a patient with macrocytosis, always review the medication list thoroughly as drug-induced causes are among the most common etiologies, even in the absence of anemia.

References

Guideline

Medication-Induced Macrocytosis

Praxis Medical Insights: Practical Summaries of Clinical Guidelines, 2025

Guideline

Guideline Directed Topic Overview

Dr.Oracle Medical Advisory Board & Editors, 2025

Research

Unexplained macrocytosis.

Southern medical journal, 2013

Research

Evaluation of macrocytosis.

American family physician, 2009

Research

Azathioprine-induced megaloblastic anemia with pancytopenia 22 years after living-related renal transplantation.

International journal of urology : official journal of the Japanese Urological Association, 1998

Research

Macrocytosis and pure RBC anemia caused by azathioprine.

American journal of diseases of children (1960), 1980

Professional Medical Disclaimer

This information is intended for healthcare professionals. Any medical decision-making should rely on clinical judgment and independently verified information. The content provided herein does not replace professional discretion and should be considered supplementary to established clinical guidelines. Healthcare providers should verify all information against primary literature and current practice standards before application in patient care. Dr.Oracle assumes no liability for clinical decisions based on this content.

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